Rett syndrome

Digitally generated DNA fragment on a dark background
Biotech

Patient put in critical condition by Neurogene gene therapy dies

Neurogene disclosed the adverse event Nov. 11 and said the patient was in critical condition Nov. 18.
Nick Paul Taylor Nov 22, 2024 3:57am
Gene editing CRISPR gene therapy

Neurogene acts as gene therapy puts person in critical condition

Nov 18, 2024 8:33am
money funding financing bank

Acadia makes $100M profit from $150M pediatric voucher sale

Nov 6, 2024 9:36am
Toxoplasma gondii

A brain parasite has been turned into drug delivery system

Jul 29, 2024 2:55pm
An artists depiction of DNA molecules made up of tiny particles

Taysha links gene therapy to motor gains in small Rett study

Jun 18, 2024 11:44am
rare diseases

FDA picks Denali, Neurogene and more for rare disease program

Jun 4, 2024 2:51pm