Ultragenyx

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Biotech

Ultragenyx tweaks gene therapy dosing to dial up efficacy

A minority of patients have come off standard-of-care drugs, leading the biotech to enroll a new cohort on a tweaked regimen to dial up the efficacy.
Nick Paul Taylor Oct 4, 2024 8:46am
Go sign green light

Ultragenyx gets green light to seek FDA approval of gene therapy

Jun 13, 2024 5:55am
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Ultragenyx, Mereo's brittle bone drug sustains fracture rate cut

Jun 12, 2024 8:55am
blood test vials

Ultragenyx's ph. 3 win for glycogen storage disease gene therapy

May 30, 2024 4:00pm
broken bone fracture break x ray skeleton

Ultragenyx, Mereo's bone disease med cuts fractures by 67%

Oct 16, 2023 12:39pm
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FDA's Marks wants more quick approvals for rare disease drugs

Jul 28, 2023 11:36am